A single intravenous rAAV injection as late as P20 achieves efficacious and sustained CNS gene therapy in Canavan mice

  • Seemin Seher Ahmed
  • , Huapeng Li
  • , Chunyan Cao
  • , Elif M. Sikoglu
  • , Andrew R. Denninger
  • , Qin Su
  • , Samuel Eaton
  • , Ana A. Liso Navarro
  • , Jun Xie
  • , Sylvia Szucs
  • , Hongwei Zhang
  • , Constance Moore
  • , Daniel A. Kirschner
  • , Thomas N. Seyfried
  • , Terence R. Flotte
  • , Reuben Matalon
  • , Guangping Gao

Research output: Contribution to journal › Article › peer-review

89 Scopus citations

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Neuroscience

Biochemistry, Genetics and Molecular Biology