Challenges of Assessing Exon 53 Skipping of the Human DMD Transcript with Locked Nucleic Acid-Modified Antisense Oligonucleotides in a Mouse Model for Duchenne Muscular Dystrophy
- Sarah Engelbeen
- , Daniel O'Reilly
- , Davy Van De Vijver
- , Ingrid Verhaart
- , Maaike Van Putten
- , Vignesh Hariharan
- , Matthew Hassler
- , Anastasia Khvorova
- , Masad J. Damha
- , Annemieke Aartsma-Rus
Research output: Contribution to journal › Article › peer-review
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