Phase 3 trial of RNAi therapeutic givosiran for acute intermittent porphyria

M. Balwani, E. Sardh, P. Ventura, P. A. Peiró, D. C. Rees, U. Stölzel, D. M. Bissell, H. L. Bonkovsky, J. Windyga, K. E. Anderson, C. Parker, S. M. Silver, S. B. Keel, J. D. Wang, P. E. Stein, P. Harper, D. Vassiliou, B. Wang, J. Phillips, A. IvanovaJ. G. Langendonk, R. Kauppinen, E. Minder, Y. Horie, C. Penz, J. Chen, S. Liu, J. J. Ko, M. T. Sweetser, P. Garg, A. Vaishnaw, J. B. Kim, A. R. Simon, L. Gouya

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