Phase 3 trial of RNAi therapeutic givosiran for acute intermittent porphyria

M. Balwani, E. Sardh, P. Ventura, P. A. Peiró, D. C. Rees, U. Stölzel, D. M. Bissell, H. L. Bonkovsky, J. Windyga, K. E. Anderson, C. Parker, S. M. Silver, S. B. Keel, J. D. Wang, P. E. Stein, P. Harper, D. Vassiliou, B. Wang, J. Phillips, A. IvanovaJ. G. Langendonk, R. Kauppinen, E. Minder, Y. Horie, C. Penz, J. Chen, S. Liu, J. J. Ko, M. T. Sweetser, P. Garg, A. Vaishnaw, J. B. Kim, A. R. Simon, L. Gouya

Research output: Contribution to journalArticlepeer-review

100 Scopus citations

Fingerprint

Dive into the research topics of 'Phase 3 trial of RNAi therapeutic givosiran for acute intermittent porphyria'. Together they form a unique fingerprint.

Medicine & Life Sciences